Gene Editing at the Bedside: From CRISPR to Patient Outcomes
In 2023, the first CRISPR-based therapy won regulatory approvals for severe sickle cell disease, transforming crisis-filled months into manageable lives. One young adult described finally planning vacations without fear. What future condition would you most want CRISPR to tackle next?
Gene Editing at the Bedside: From CRISPR to Patient Outcomes
Base and prime editing promise subtler corrections, like changing a single letter linked to dangerous cholesterol levels. Early trials are careful, small, and methodical. Should we prioritize rare, devastating diseases first, or target widespread risks to maximize population health?